Tag Archives: FDA

Cord Blood, a life line

We are living in truly amazing times as scientists are just beginning to understand the power of stem cells. In particular, cord blood stem cells are providing new hope to cancer patients throughout the world. At Save the Cord Foundation, … Continue reading

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Baby Steps in Congress

Getting things done for childhood cancer in Congress is not easy. For one, even as a community, we have very little political clout. One of the best things going for us is that  we have the Childhood Cancer Caucus in … Continue reading

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Immunotherapy

I am not sure how many people outside of the cancer research community know this, but it is well recognized that the human body is equipped to fight off cancer on its own. The same immune system that we have … Continue reading

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Compassionate Use

You may remember the #SaveJosh news articles in the spring of 2014 where little Josh Hardy’s family mounted, as a last ditch effort, a social media campaign to get him into a clinical trial that St. Jude’s doctors said was … Continue reading

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The Fault in Our Systems

by Nathan Traller, Nathalie’s father Editor’s Note: Nathan’s daughter was diagnosed with Aveolar Soft Part Sarcoma (ASPS) two years ago and he has been fighting to get her into a possible life saving clinical trial for PD1 and PDL1. Time … Continue reading

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30% Funding Cuts

Just weeks before she died of a brain tumor, ten-year-old Gabriella Miller put it best. When asked what message she would give to the nation’s political leaders about the need for children’s cancer research, she responded in a YouTube video … Continue reading

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Thank You, American Cancer Society

In the past, I have been a huge critic of the American Cancer Society and in September, I wrote a very inflamed blog  about all that I felt was  wrong with the American Cancer Society’s (ACS) involvement with childhood cancer.  … Continue reading

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Let’s Push Buttons

Would you believe?: 96% of all clothing sold is for adults. 96% of all breakfast cereals are consumed by adults. 96% of all bicycle helmets are worn by adults. 96% of all cancer research conducted by the National Cancer Institute … Continue reading

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We need more than just research

A mother noticed that her six year-old son’s eyelids were not closing normally and when he walked, he was slightly off balance.  A few days later, his parents’ worst nightmare became a reality; they were told that their son has … Continue reading

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The FDA and Childhood Cancer – Part 2

This is part 2 of the Jonathan Agin series, “Childhood Cancer – My Road Map” Being sent to an emergency room to have a CT scan performed on your two-year-old child is frightening. Being brought into a small cramped room … Continue reading

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Engaging the Pharmaceutical Industry – Part 1

This is beginning of a four part series by Jonathan Agin, an attorney and well known childhood cancer advocate (www.jonathanagin.com) in Washington, DC. He is married to Neely Agin and is the father of Alexis, Gabriel Agin and Trevor Agin. Alexis was … Continue reading

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The Funding Conundrum for Pediatric Cancer

My grandson, at 15 months of age, was diagnosed with high risk neuroblastoma. He is a survivor.  Although, he  endured an incredible six year long journey, this story is not about him,  his family, the changes in their lives, or … Continue reading

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Tissue Donation – The last thing any parent wants to give

Progress, unfortunately is sometimes forged from the fires of pain mixed with strength, courage, passion and determination.  Nancy Goodman has such a story.  Nancy made a donation that no parent ever wants to give.   “My son, Jacob, was a beautiful, … Continue reading

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Cancer Drug’s Valley of Death – Where is it, What is it?

To truly understand the problems with development of drugs specific to childhood cancer, and rare disease in general, examine the FDA’s Therapeutic Development Pipeline below.  The pipeline represents the normal development of an average drug.  The average successful drug will … Continue reading

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