Build on Success with GMKF2

In 2014, Congress passed  The Gabriella Miller Kids First Pediatric Research Act and President Obama signed it into law the very same year. The act was intended to be a 10-year program. With $75 million of non-taxpayer funding provided by the act over the past six years, the National Institutes of Health (NIH) Common Fund established the very successful Gabriella Miller Kids First Pediatric Research Program (Kids First).  Another $50 million is expected to be appropriated over the remaining four years of the Act.



The Kids First Program fosters collaborative research to uncover the genetic etiology of childhood cancer and structural birth defects.  In pursuit of this goal, NIH developed the Gabriella Miller Kids First Pediatric Data Resource Center (Kids First Data Resource Center), and is in Ekd-QkhWAAIjscGthe process of expanding a public-facing, web-based portal that allows researchers to search, access, aggregate, analyze, and share annotated genomic sequence, variant, and phenotypic datasets. This resource is of high value for the pediatric research community and will facilitate analyses across diverse conditions to uncover shared developmental pathways.  Under this program, more than two-dozen pediatric research focused laboratories have generated vital genomic data that will be shared with the entire research community.

The overall goal is to help researchers understand the underlying mechanisms of these conditions leading to more NotSamerefined diagnostic capabilities and ultimately more targeted therapies or interventions.  This First Act is just the beginning, we must continue and enhance this vital work, because while cancer is the single leading cause of death by disease among American children,  currently only 4%  of the National Cancer Institute’s $4.9 billion budget goes towards development of cures and treatments for childhood cancer.  Because of limited research in the past 30 years, only 4 drugs have been developed exclusiverly to treat childhood cancer.

With H.R. 6556 – The Gabriella Kids First Research Act 2.0, again with non-taxpayer funding, we will be able to expand this program to develop a truly comprehensive shared-data resource for scientists researching the majority of pediatric cancers and structural birth defects, and support development of computational tools to analyze these very large, complex genomic, and clinical data sets.

The Gabriella Miller Kids First Research Act 2.0 (H.R. 6556) would redirect penalties levied againstUntitled-2 pharmaceutical manufacturers by the U.S. Securities and Exchange Commission (SEC) for violating the Foreign Corrupt Practice Act (FCPA). The funds from the penalties would be transferred to the Kids First Pediatric Research Program (Kids First) at the National Institutes of Health (NIH). There have been consistent and large civil sanctions leveraged against pharmaceutical companies since 2013 – hundreds of millions of dollars from six violations alone. With this legislation, penalties from pharmaceutical companies that break the law would be channeled directly to critical medical research.

Representatives Tom Cole (R-OK-04), Peter Welch (D-VT-At Large), and Gus Bilirakis (R-FL-12) joined Representative Jennifer Wexton (D-VA-10) who introduced this legislation. In addition, 24 Representatives (sse below)  have recently cosponsored. As of this writing, we already have over 200 foundations and organizations and more than 1,000 advocates covering all 50 states, who have signed a letter of support for this new bill.

Your support is essential now to build upon the successful work that has already been done and to expand and enhance our capabilities in the future. Please consider cosponsoring H.R. 6556 – Kids First Research Act 2.0.

Ellyn Miller, always Gabriella’s mom

36 Cosponsors (23D, 13R)

Sponsor/Cosponsor Joined/Withdrawn On Assigned Committees
D Wexton, Jennifer [D-VA10] Primary Sponsor
Financial Services
R Bilirakis, Gus [R-FL12] Original Cosponsor
Energy and Commerce
D Welch, Peter [D-VT0] Original Cosponsor
Energy and Commerce
D O’Halleran, Tom [D-AZ1] May 22, 2020
Energy and Commerce
R McKinley, David [R-WV1] May 27, 2020
Energy and Commerce
R McMorris Rodgers, Cathy [R-WA5] Jun 4, 2020
Energy and Commerce
R Mullin, Markwayne [R-OK2] Jun 11, 2020
Energy and Commerce
R Flores, Bill [R-TX17] Jun 15, 2020
Energy and Commerce
R Brooks, Susan [R-IN5] Jul 6, 2020
Energy and Commerce
D Peters, Scott [D-CA52] Jul 20, 2020
Energy and Commerce
R Olson, Pete [R-TX22] Jul 27, 2020
Energy and Commerce
D Barragán, Nanette [D-CA44] Sep 1, 2020
Energy and Commerce
D Soto, Darren [D-FL9] Sep 15, 2020
Energy and Commerce
D Kelly, Robin [D-IL2] Sep 30, 2020
Energy and Commerce
D Tonko, Paul [D-NY20] Oct 16, 2020
Energy and Commerce
D Blunt Rochester, Lisa [D-DE0] Oct 27, 2020
Energy and Commerce
D Matsui, Doris [D-CA6] Oct 27, 2020
Energy and Commerce
D San Nicolas, Michael [D-GU0] Jun 4, 2020
Financial Services
D Pressley, Ayanna [D-MA7] Jul 6, 2020
Financial Services
R Riggleman, Denver [R-VA5] Oct 16, 2020
Financial Services
R Wagner, Ann [R-MO2] Oct 27, 2020
Financial Services
R Cole, Tom [R-OK4] Original Cosponsor
D Jackson Lee, Sheila [D-TX18] May 8, 2020
D Cohen, Steve [D-TN9] Jun 11, 2020
R Grothman, Glenn [R-WI6] Jun 24, 2020
D Spanberger, Abigail [D-VA7] Jun 24, 2020
D Evans, Dwight [D-PA3] Jul 6, 2020
D Harder, Josh [D-CA10] Jul 16, 2020
R Wittman, Robert [R-VA1] Jul 29, 2020
D Connolly, Gerald [D-VA11] Aug 18, 2020
D Cox, TJ [D-CA21] Sep 1, 2020
D Hastings, Alcee [D-FL20] Sep 1, 2020
D Correa, Luis [D-CA46] Sep 15, 2020
D Speier, Jackie [D-CA14] Sep 15, 2020
D Scanlon, Mary [D-PA5] Sep 30, 2020
D Takano, Mark [D-CA41] Oct 16, 2020
R Yoho, Ted [R-FL3] Oct 16, 2020